Christopher VelonaOct 17, 20192 minCalifornia Senate Approves Wilk’s Batten Disease Awareness Weekend Bill
Christopher VelonaOct 17, 20191 minTeen With Neurological Disorder to Throw First Pitch at Dodgers Game
Christopher VelonaSep 3, 20196 minAmicus CEO John Crowley Outlines Progress in Batten, Pompe, Fabry Therapies
Christopher VelonaJun 12, 20195 minWhole-Genome Sequencing Plus AI Yields Same-Day Genetic DiagnosesBack in April 2003, when the international Human Genome Project successfully completed the first reference sequence of the human DNA blue...
Christopher VelonaJun 7, 20197 minAmicus Therapeutics Acquires Gene Therapy Portfolio Amicus Therapeutics Acquires Gene Therapy Portfolio of Ten Clinical and Pre-Clinical Stage AAV Programs in Neurologic Lysosomal Storage D...
Christopher VelonaJun 6, 20192 minFamily Battles Rare Batten Disease, Accepting Donations For Accessible HomeST. PAUL, Minn. (WCCO) — A family that has two kids with a rare terminal disorder is trying to remove barriers and make life easier at ho...
Christopher VelonaJun 6, 20195 minClinical Trial Set to Start for CLN1 Batten DiseaseOn May 21, Abeona Therapeutics announced the go-ahead from the Food and Drug Administration (FDA) for a clinical trial to test a gene the...
Christopher VelonaJun 6, 20192 minWhat is Batten Disease?Batten disease, or Neuronal Ceroid Lipofuscinosis (NCL), is a family of rare diseases caused by autosomal recessive genetic mutations res...
